New study shows that dysfunction of protective immune cells in GI tract may contribute to onset of inflammation in Crohn's disease.

A research team led by Mount Sinai has uncovered mechanisms of abnormal immune cell function that may lead to Crohn's disease ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

What is Guillain-Barré syndrome? Guillain-Barré syndrome (GBS) is also called acute inflammatory demyelinating polyradiculoneuropathy (AIDP). It's a neurological disorder in which the body's immune ...

(RTTNews) - Acadia Pharmaceuticals Inc. (ACAD) announced the publication of clinical data from the open-label DAFFODIL study, which evaluated the long-term safety and efficacy of DAYBUE or ...

Acadia Pharmaceuticals Inc. today announced that the journal Med published results from the open-label study, DAFFODILtm, evaluating the safety, tolerability and exploratory efficacy of DAYBUE® ...

DAYBUE, a synthetic analog of insulin-like growth factor 1, is designed to treat Rett syndrome, although its exact therapeutic mechanism is not fully understood. It is available as an oral ...

Clinical Data from Open-Label DAFFODIL™ Study Evaluating Long-term Safety of DAYBUE® (trofinetide) in Patients with Rett Syndrome Published in Med -- Study supported FDA and Health Canada ...

such as Rett syndrome or Angelman syndrome, or even more complex neurodevelopmental conditions. It also provides instant medical recommendations, directing patients to specialized departments and ...

We remain encouraged by our productive, ongoing discussions with the FDA through the Regenerative Medicines Advanced Therapy or RMAT mechanism ... of patients with Rett syndrome using a minimally ...

Chronic fatigue syndrome — also known as myalgic encephalomyelitis ... but more research is necessary to establish the mechanism behind this. According to the Office on Women’s Health, females ...