Unearthing an old stuffed animal led columnist Alyssa Silva to recall the memory of realizing how different her childhood was ...

Data from the SAPPHIRE study formed the basis of Scholar Rock's U.S. Food and Drug Administration request to approve apitegromab for SMA.

Columnist Ari Anderson reflects on the memories that made his old house so special and looks forward to making many more in ...

After five years of Evrysdi, people with SMA types 2 and 3 are continuing to show stabilization and improvement in motor ...

Children with SMA given the gene therapy Zolgensma in infancy are maintaining motor milestones after up to 10 years, new ...

Columnist Sherry Toh thanks the dedicated nurses who've attended to her at various hospitals and at home over the years.

This weekend kicked off the MDA annual Clinical & Scientific Conference, bringing together the neuromuscular disease ...

Winters are hard for columnist Alyssa Silva — as is life with SMA. She reminds herself of the importance of finding light in ...

SMA patients want PROMs that focus on more than physical function, and that also assess mental health, sexual function, sleep ...

A study based on a survey of 50 adults linked poorer quality sleep with more depressive symptoms and respiratory issues in ...

OAV101 IT, a version of the gene therapy Zolgensma (onasemnogene abeparvovec-xioi) that’s administered into the spinal canal, can be safely given to people with spinal muscular atrophy (SMA) who were ...

Thanks to the 21st Century Cures Act, columnist Brianna Albers tends to needlessly stress about lab results her doctor hasn't yet reviewed.