A new gene-targeting strategy that boosts a crucial brain protein could pave the way for the first effective treatment for ...

A team of researchers at Baylor College of Medicine and the Duncan Neurological Research Institute (Duncan NRI) at Texas ...

Researchers have discovered a new way to increase a key brain protein damaged in Rett syndrome, a rare genetic disorder that affects thousands of children worldwide. Early studies in mice and ...

A team of researchers at Texas Children's Duncan Neurological Research Institute (NRI) and Baylor College of Medicine report ...

Gene therapy may offer hope for people with a rare childhood disease called Rett syndrome. Around one in 10,000 girls are born each year with Rett syndrome, a rare genetic condition that impacts brain ...

Rett syndrome is a rare developmental disorder, most often due to a mutation in the MECP2 gene on the X chromosome, but it’s not usually inherited. Advances in genetics have launched a new era in ...

The Rett Syndrome Research Trust (RSRT), the organization singularly focused on curing Rett syndrome, today announced 2025 research awards totaling $6.4 million, further advancing genetic medicine ...

A team of researchers at Texas Children’s Duncan Neurological Research Institute (NRI) and Baylor College of Medicine report ...

BENGALURU: Awareness about rare diseases can sometimes prevent serious conditions from being overlooked. One such condition is Rett Syndrome, a rare neurological disorder that many people aren’t ...

IRSF investment positions organization at the forefront of early-stage Rett research as genomic medicine reshapes rare ...

Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...