Rett syndrome is a devastating rare genetic childhood disorder primarily affecting girls. Merely 1 out of 10,000 girls are ...

Using an AI-driven drug discovery process, the drug known as vorinostat was identified as a promising treatment for Rett ...

More information: Osman Sharifi et al, Sex-specific single cell-level transcriptomic signatures of Rett syndrome disease ...

The pivotal trial for Neurogene's Rett syndrome gene therapy makes use of baseline controls and a rigorous endpoint that ...

Then, on February 1, 2023, Jayla was diagnosed with Rett syndrome. Two months after giving birth to their daughter, Jayla, Shelly Balboa and her partner, Joseph, noticed the left side of their ...

For Kassie and Brian Morell, this disorder has hit doubly hard as their identical twin daughters were diagnosed at two and a half years old. As October is Rett Syndrome Awareness Month, the Morell ...