This means the other half of the cells with a wild-type copy of MECP2 inherited from the other parent expresses normal MeCP2 ...

The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died, but that won't cause the study to be halted. The FDA has allowed the ...

I’m thrilled to join the Board of Trustees and get even closer to the Reverse Rett mission,” says Amy Gilliland. “As a parent of a child living with Rett syndrome—like so many others leading and ...

Neurotech said Rett syndrome was a rare genetic neurological and developmental disorder and is almost exclusively the result of mutation(s) in the methyl CpG binding protein 2 (MECP2) gene located on ...

The Blue Bird Circle Rett Center at Baylor College of Medicine is composed of a multidisciplinary team of health professionals. Several BCM physicians are involved clinically at the Blue Bird Circle ...

Clinical Data from Open-Label DAFFODIL™ Study Evaluating Long-term Safety of DAYBUE® (trofinetide) in Patients with Rett Syndrome Published in Med -- Study supported FDA and Health Canada ...

(RTTNews) - Acadia Pharmaceuticals Inc. (ACAD) announced the publication of clinical data from the open-label DAFFODIL study, which evaluated the long-term safety and efficacy of DAYBUE or ...