She slept in hospital intensive care units and navigated family outings with a breathing machine – all for her late son, who ...
The mother of a four-year-old boy with a rare muscle disease says screening newborn babies for the condition could "save ...
A couple whose son died from a rare genetic condition are encouraging others to take part in screening which they say could ...
Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
On January 4, former Little Mix singer Jesy Nelson took to Instagram to reveal that her twins have been diagnosed with spinal muscular atrophy (SMA) type 1, which is a genetic neuromuscular condition ...
More than two years after the Government committed to adding SMA to newborn testing, families are still waiting ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
The 34-year-old singer recently shared the devastating news that her children have Spinal Muscular Atrophy Type 1, which ...
The Independent on MSN
What is spinal muscular atrophy?
What is SMA? The rare genetic condition that Jesy Nelson’s twins have - Former Little Mix star revealed her twin daughters had been diagnosed with Spinal Muscular Atrophy (SMA) Type 1 ...
A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...
The singer shared an emotional update about her twins’ health on Sunday.
LITTLE Mix star Jesy Nelson has revealed that her baby twins have been diagnosed with a severe form of Spinal Muscular Atrophy. In a heart-breaking Instagram post, the singer said her daughters could ...
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